Research Row: Strategies to Restore Dystrophin

Annemieke Aartsma-Rus, PhD, University of Leiden (Moderator)

Avidity Biosciences – AOC 1044: Henry Nchienzia, PhD, Avidity Biosciences

Biomarin – BMN 351: Peter Velzquez, PhD, BioMarin Pharmaceutical Inc.

Dyne Therapeutics – DYNE-251: John Cox, MBA, Dyne Therapeutics

Entrada Therapeutics – ENTR-601-44: Mahasweta Girgenrath, PhD, Entrada Therapeutics

NS Pharma – NS-089 / NS-050: Robert Crozier, PhD, NS Pharma

Pepgen – PGN-EDO51: Bassem Morcos, MD, Pepgen

PTC Therapeutics – Ataluren: Jonathan Blaize, PhD, PTC Therapeutics

Sarepta Therapeutics – SRP-5051: Karin Lucas, PhD, Sarepta Therapeutics

Wave Life Sciences – WVE-N531: Angel Angelov, MD, MBA, Wave Life Sciences