For over twenty five years, Parent Project Muscular Dystrophy has been committed to exploring and supporting innovative therapeutic possibilities. We take a cutting-edge approach to accelerate finding treatments that will end Duchenne for every single person impacted by the disease. And today, the Duchenne therapeutic pipeline has never been so full of promise, with over 35 potential treatments in various stages of testing. However, along with this promise, we know it can sometimes be difficult to keep track of the latest progress for each therapy in the pipeline.
PPMD provides a variety of resources for learning about potential treatments and clinical trials for people with Duchenne and Becker, as well as female carriers. Today, we are excited to launch our new interactive drug development pipeline to further help the community stay up-to-date on all therapies that are currently in development.
Check out PPMD’s interactive pipeline and click on any drug to learn more about therapies in development for Duchenne, including:
- A summary of therapeutic strategies and what they are aimed at addressing
- The current phase and status of related clinical trials
- The latest research news
- A video library providing quick access to PPMD webinars and presentations
There is a momentum in the Duchenne research pipeline, the likes of which we have never seen before. And it’s never been more important to ensure that the path to progress is clear, so that safe and effective therapies can reach the people who need them quickly and affordably. PPMD will continue to actively engage in the drug development pipeline, supporting innovative therapies from the early, discovery stage of the process through our community’s first approvals and the complicated access environment that follows.
The Duchenne Registry: Keeping You Up-to-Date on All Clinical Trials
One of the easiest and most effective ways you can stay up-to-date with actively recruiting clinical trials and research studies is by joining The Duchenne Registry and keeping your profile up to date. The Duchenne Registry is the only Duchenne-specific registry that enables families to receive targeted recruitment information — soon in the palm of your hand!
Once you register and complete the surveys, the Registry will let you know when you or your child appear to match the inclusion criteria for research studies and clinical trials. The data you contribute also helps both industry partners and researchers know essential information for planning trials and studies, such as the size of the Duchenne population available, geographic concentration of patients, and clinical site cohort size. This increases our community’s access to studies and potential therapies.
The new Duchenne Registry App will be live next week — please sign up to JOIN when it is launched! Stay tuned because detailed app instructions will be coming to you via email and will also be available on The Duchenne Registry website.Visit The Duchenne Registry