Restoring Dystrophin via Exon Skipping Strategies
AOC 1044 – Mark Stahl, MD (Avidity Biosciences)
BMN 351 – Dave Jacoby MD, PhD (BioMarin Pharmaceutical Inc.)
DYNE-251 – Ash Dugar, PhD, MBA (Dyne Therapeutics)
ED051 – Michelle Mellion, MD (PepGen, Inc.)
ENTR-601-44 – Nerissa Kreher, MD, MBA (Entrada Therapeutics)
SRP-5051 – Teji Singh, MD (Sarepta Therapeutics)
WVE-N531 – Mike Panzara, MD, MPH (Wave Life Sciences)