Gene Therapy Trials (PPMD 2019 Conference) AGENDA 0:00 – Gene Therapy Trials Moderator: Richard Klein 2:08 – Solid – Genevieve A. Laforet, MD, PhD 24:02 – Pfizer – Michael Binks, MD 46:42 – Sarepta – Doug Ingram 1:11:24 – Q&A 1:42:25 – POLLING QUESTIONS 7 years ago 2019 PPMD Annual Conference,Conferences & Meetings You may also like 2:12:40 Gene Therapy Town Hall – PPMD 2023 Annual Conference 3 years ago 2023 PPMD Annual Conference,Conferences & Meetings 34:56 Keynote: Change How You See, See How You Change – PPMD 2023 Annual Conference 3 years ago 2023 PPMD Annual Conference,Conferences & Meetings 36:32 Keynote: Priorities or Finding Your “US” – PPMD 2023 Annual Conference 3 years ago 2023 PPMD Annual Conference,Conferences & Meetings 18:50 Duchenne Landscape Now Research & Trials Progress – PPMD 2023 Annual Conference 3 years ago 2023 PPMD Annual Conference,Conferences & Meetings 19:52 Welcome to Dallas! Where We are and What to Expect – PPMD 2023 Annual Conference 3 years ago 2023 PPMD Annual Conference,Conferences & Meetings 48:08 Learning and Behavior Breakout Session: Teens/Adult — PPMD 2022 Annual Conference 4 years ago 2022 PPMD Annual Conference,Conferences & Meetings 58:20 Learning & Behavior Breakout Session: Late Childhood & Tweens – PPMD 2022 Annual Meeting 4 years ago 2022 PPMD Annual Conference,Conferences & Meetings 1:04:31 Learning and Behavior Breakout Session: Early Childhood — PPMD 2022 Annual Conference 4 years ago 2022 PPMD Annual Conference,Conferences & Meetings «1…89101112…30»Page 10 of 30