Gene Correction (PPMD 2019 Conference) 0:00 – Gene Correction Moderator: Richard Klein 1:16 – PTC – Richard Able Jr., PhD 20:30 – Sarepta – Gilmore O’Neill, M.B., M.M.SC. 38:57 – Wave – Michael Panzara, MD, MPH 59:13 – NS Pharma – Leslie Magnus, MD 1:10:36 – Q&A 1:23:36 – POLLING QUESTIONS 2019 PPMD Annual Conference,Conferences & Meetings 6 years ago You may also like 1:02:36 KEYNOTE: Destigmatizing Disability — PPMD 2022 Annual Conference 3 years ago 2022 PPMD Annual Conference,Conferences & Meetings 21:05 Duchenne 101 (Being Diagnosed & The Words You Hear) — PPMD 2022 Annual Conference 3 years ago 2022 PPMD Annual Conference,Conferences & Meetings 1:45:26 Duchenne 101 (Genetics, Comprehensive Care & Clinical Trials) – PPMD 2022 Annual Conference 3 years ago 2022 PPMD Annual Conference,Conferences & Meetings 18:47 Duchenne 101 (Welcome & Session Overview) — PPMD 2022 Annual Conference 3 years ago 2022 PPMD Annual Conference,Conferences & Meetings 16:17 Where Have We Been & Where We Are We Going 4 years ago 2021 PPMD Virtual Conference: Live Sessions,Conferences & Meetings 16:43 Power in Advocacy 4 years ago 2021 PPMD Virtual Conference: Live Sessions,Conferences & Meetings 47:16 The Ins & Outs of GI Health & Nutrition 4 years ago 2021 PPMD Virtual Conference: Live Sessions,Conferences & Meetings 53:24 A Patient’s Take on Pulmonary Management 4 years ago 2021 PPMD Virtual Conference: Live Sessions,Conferences & Meetings «1…1213141516…28»Page 14 of 28