Gene Correction (PPMD 2019 Conference) 0:00 – Gene Correction Moderator: Richard Klein 1:16 – PTC – Richard Able Jr., PhD 20:30 – Sarepta – Gilmore O’Neill, M.B., M.M.SC. 38:57 – Wave – Michael Panzara, MD, MPH 59:13 – NS Pharma – Leslie Magnus, MD 1:10:36 – Q&A 1:23:36 – POLLING QUESTIONS 6 years ago 2019 PPMD Annual Conference,Conferences & Meetings You may also like 1:04:31 Learning and Behavior Breakout Session: Early Childhood — PPMD 2022 Annual Conference 3 years ago 2022 PPMD Annual Conference,Conferences & Meetings 1:27:21 Care Breakout Session: Teen and Adult Care — PPMD 2022 Annual Conference 3 years ago 2022 PPMD Annual Conference,Conferences & Meetings 1:16:04 Care Breakout Session: Late Childhood & Tweens – PPMD 2022 Annual Conference 3 years ago 2022 PPMD Annual Conference,Conferences & Meetings 1:28:44 Care Breakout Session: Early Childhood — PPMD 2022 Annual Conference 3 years ago 2022 PPMD Annual Conference,Conferences & Meetings 1:30:45 Panel Discussion: Looking Ahead to Combination Therapies — PPMD 2022 Annual Conference 3 years ago 2022 PPMD Annual Conference,Conferences & Meetings 1:22:12 Caring for the Caregiver of Teens & Adults Living with Duchenne — PPMD 2022 Annual Conference 3 years ago 2022 PPMD Annual Conference,Conferences & Meetings 28:44 Strategies for Mitigating Inflammation and Fibrosis — PPMD 2022 Annual Conference 3 years ago 2022 PPMD Annual Conference,Conferences & Meetings 17:46 Late Breaking News: Capricor / Cap-1002 — PPMD 2022 Annual Conference 3 years ago 2022 PPMD Annual Conference,Conferences & Meetings «1…89101112…28»Page 10 of 28