About PPMD
Events
News
About Duchenne
What is Duchenne?
Signs & Symptoms
Duchenne Diagnosis
Progression
Interpreting CK Levels
What is Becker?
Signs and Symptoms
Becker Diagnosis
Understanding Genetics
Genetic Causes
Types of Genetic Variants
Genetic Testing
Genetic Counseling
Carriers
Newborn Screening
Newly Diagnosed?
What You Need to Know
Join the Community
Things to Do Now
Decode Duchenne Free Genetic Testing Program
Care
For Families
For Newly Diagnosed
Assembling a Care Team
Transition of Care Through Adulthood
Community Resource Center
Knight Hacks: Everyday Tips & Tricks for Families
School Resources
Living Duchenne Podcast
Approved Therapies for Duchenne Muscular Dystrophy
Duchenne Care Guidelines
By Areas of Care
By Stage of Progression
Emergency Care
Surgery & Anesthesia Precautions
Find a Certified Duchenne Care Center
Certified Duchenne Care Center Application
Access & Coverage Resources
For New Therapies
For Medical Equipment
Support & Care Materials
Webinar & Video Library
PPMD For You: Schedule a One-To-One Meeting for Personalized Support
For Adults / Young Adults
For Carriers
For Healthcare Professionals
For Educators
Our Strategy & Impact
Advocacy
Our Strategy & Impact
Legislation & Public Policy
Regulatory
Access & Coverage
Become an Advocate
Ongoing Initiatives
Insurance Access & Coverage Resources
Duchenne Newborn Screening Action Center
Take Action
Current Action Alerts
Advocacy Conference
Advocacy Results
Advocacy News
Research
Current Research
Our Strategy & Impact
Therapeutic Approaches
Drug Development Pipeline
Understanding Clinical Trials
Explore Clinical Trials
Gene Therapy Hub
The Duchenne Registry
PPMD Venture Pathways
For Researchers & Industry
Recruit for Research
Research Grant Opportunities
Drug Development Roundtable
Resources
Get Involved
Donate
Make a Donation
Matching Gifts
Find Sponsorship Opportunities
PPMD Merchandise
Fundraise
Race to End Duchenne
DIY Fundraising
Coach To Cure MD
World Duchenne Awareness Day
Bad Shirt Friday
Advocate
Join The Duchenne Registry
Connect With the Community
Find a Local Connect Group
The PAAC: Teens & Adults with Duchenne
Tweens (ages 9-14)
Siblings
Dads
Grandparents
PPMD Lighthouse Workshops
Attend Events
Annual Conference
PPMD Together
Advocacy Conference
See all events
Join our email List
Duchenne Registry
Donate
Duchenne Registry
Donate
About Duchenne
What is Duchenne?
Signs & Symptoms
Duchenne Diagnosis
Progression
Interpreting CK Levels
What is Becker?
Signs and Symptoms of Becker
Becker Diagnosis
Understanding Genetics
Genetic Causes
Types of Genetic Variants
Genetic Testing
Genetic Counseling
Carriers
Newborn Screening
Newly Diagnosed?
What You Need to Know
Join the Community
Things to Do Now
Decode Duchenne Program
Care
For Families
For Newly Diagnosed
Assembling a Care Team
Transition of Care Through Adulthood
Community Resource Center
PPMD Knight Hacks
School Resources
Living Duchenne Podcast
Approved Therapies for Duchenne Muscular Dystrophy
Duchenne Care Guidelines
By Areas of Care
By Stage of Progression
Emergency Care
Surgery & Anesthesia Precautions
Find a Certified Care Center
Certified Duchenne Care Center Application
Access & Coverage Resources
For New Therapies
For Medical Equipment
Support & Care Materials
Webinar & Video Library
PPMD For You: Schedule a One-To-One Meeting for Personalized Support
For Adults / Young Adults
For Carriers
For Healthcare Providers
For Educators
Our Strategy & Impact
Advocacy
Our Strategy & Impact
Legislation & Public Policy Advocacy
Regulatory
Access & Coverage
Become an Advocate
Ongoing Initiatives
Insurance Access & Coverage Resources
Duchenne Newborn Screening Action Center
Take Action
Current Action Alerts
Advocacy Conference
Advocacy Results
Advocacy News
Research
Current Research
Our Strategy & Impact
Therapeutic Approaches
Drug Development Pipeline
Understanding Clinical Trials
Explore Clinical Trials
PPMD’s Gene Therapy Hub
The Duchenne Registry
PPMD Venture Pathways
For Researchers & Industry
Recruit for Research
Research Grant Opportunities
PPMD’s Drug Development Roundtable
Resources
Get Involved
Donate
Matching Gifts
Find Sponsorship Opportunities
PPMD Merchandise
Fundraise
Race to End Duchenne
DIY Fundraising
Coach To Cure MD
World Duchenne Awareness Day
Advocate
Join the Duchenne Registry
Connect With the Community
Find a Local PPMD Connect Group
The PAAC: Teens & Adults with Duchenne
Tweens (ages 9-14)
Siblings
PPMD Lighthouse Workshops
Dads
Grandparents
Attend Events
Annual Conference
PPMD Together
Advocacy Conference
See all events
Join our email List
About PPMD
Events
News
User Videos
Home
❯
User Videos
521 videos found
1:01:30
Webinar: Community Update with ITF Therapeutics – Introducing DUVYZAT™ (givinostat)
2 years ago
Research & Clinical Trial Webinars
,
Webinars
duvyzat
,
feature
,
givinostat
,
itf therapeutics
45:03
Webinar: Sarepta Therapeutics – Data update from MOMENTUM study, SRP-5051
2 years ago
Research & Clinical Trial Webinars
,
Webinars
sarepta
39:33
Webinar: NS Pharma – Overview of New Exon Skipping Trials: Brogidirsen and NS-050/NCNP-03
2 years ago
Research & Clinical Trial Webinars
,
Webinars
ns pharma
52:15
Overview of WVE-N531 and the FORWARD-53 Clinical Trial with Wave Life Sciences
2 years ago
Research & Clinical Trial Webinars
,
Webinars
wave life sciences
,
WVE-N531
29:09
PTC Therapeutics — EMFLAZA® Landscape in 2024
2 years ago
Care Webinars
,
Webinars
emflaza
,
ptc therapeutics
53:59
Dyne Therapeutics — Advancing DYNE-251, an Investigational Medicine for DMD
2 years ago
Research & Clinical Trial Webinars
,
Webinars
dyne therapeutics
,
DYNE-251
1:00:58
Navigating Steroid Choices: Understanding the Process, Pathways, and Policies
2 years ago
Care Webinars
,
Webinars
steroids
1:03:41
Community Update with Solid Biosciences on the New INSPIRE DUCHENNE Clinical Study of SGT-003
2 years ago
Research & Clinical Trial Webinars
,
Webinars
gene therapy
,
sgt-003
,
solid biosciences
59:54
Overview of Topline Results from Phase 3 EMBARK Study
2 years ago
Research & Clinical Trial Webinars
,
Webinars
sarepta
25:01
Advocating for Access: Overview of Medicaid DUR and P&T Meetings
2 years ago
Care Webinars
,
Webinars
feature
,
insurance
,
medicaid
54:28
Capricor Therapeutics: CAP-1002 HOPE-3 Program Update
2 years ago
Research & Clinical Trial Webinars
,
Webinars
capricor
13:45
Duchenne Community Advocates to Add Duchenne to Minnesota’s Newborn Screening Panel
2 years ago
General Information
newborn screening
49:31
Edgewise Therapeutics: A Novel Approach Designed to Protect Muscle in Becker Muscular Dystrophy
2 years ago
Research & Clinical Trial Webinars
,
Webinars
edg-5506
,
edgewise
59:38
Supporting Families Through Decision Making
2 years ago
Care Webinars
,
Webinars
palliative care
52:31
Affinity Duchenne™ and Affinity Beyond™: Updates on Investigational RGX-202 from REGENXBIO
2 years ago
Research & Clinical Trial Webinars
,
Webinars
31:23
Advocating for Access: Insurance 101
3 years ago
Care Webinars
,
Webinars
«
1
…
5
6
7
8
9
…
33
»
Page 7 of 33
Research
Advocacy
Care
Community
Join Our Mailing List
Instagram
This field is for validation purposes and should be left unchanged.
Email